Results of a Global Phase 3, Randomized, Double-Blind, Placebo-Controlled Trial Evaluating the Efficacy and Safety of Sebelipase Alfa as an Enzyme Replacement Therapy in Children and Adults with Lysosomal Acid Lipase Deficiency
Articles > Abstract · 2014
Authors: Manisha Balwani, Barbara Burton, Ivo Baric, Martin Bialer, Thomas A. Burrow, Carmen Camarena Grande, Mahmut ÇOKER, Alejandra Consuelo Sanchez, Patrick Deegan, Maja Di Rocco, Gregory M. Enns, Richard W. Erbe, Fatih Suheyl Ezgu, Francois Feillet, Can Ficicioglu, Katryn N. Furuya, Norberto Bernardo Guelbert, John Kane, Maria Kostyleva, Christina M. Laukaitis, Vera Malinova, Eugen Mengel, Elaine Murphy, Edward G. Neilan, Scott Nightingale, Jose Pastor Rosado, Heidi Peters, Yusof Rahman, Maurizio Scarpa, Karl Otfried Schwab, Vratislav Smolka, Joanna Taybert, Vassili Valayannopoulos, Marnie Wood, Mikio Zeniya, Yijun Yang, Stephen Eckert, Sandra Rojas-Caro, Anthony G. Quinn
HEPATOLOGY, Journal Indexed in SCI Expanded, International, 2014, vol 60