EFFICACY AND SAFETY OF SEBELIPASE ALFA IN CHILDREN AND ADULTS WITH LYSOSOMAL ACID LIPASE DEFICIENCY: RESULTS OF A PHASE 3 TRIAL
Conference paper > Summary Text · 2015
Authors: S. ROJAS-CARO, I. BARIC, C. CAMARENA GRANDE, Mahmut ÇOKER, P. Deegan, M. DIROCCO, F. S. Ezgu, F. FEILLET, V. MALINOVA, E. MENGEL, E. Murphy, J. PASTOR ROSADO, Y. RAHMAN, M. SCARPA, K. O. SCHWAB, V. SMOLKA, J. TAYBERT, V. VALAYANNOPOULOS, Y. YANG, A. QUINN
50th International Liver Congress of the European-Association-for-the-Study-of-the-Liver, Austria, International, Verbal, Summary Text, 2015-2015, WoS, vol 62, pp S811-S811