EFFICACY AND SAFETY OF SEBELIPASE ALFA IN CHILDREN AND ADULTS WITH LYSOSOMAL ACID LIPASE DEFICIENCY: RESULTS OF A PHASE 3 TRIAL

Conference paper > Summary Text · 2015

Authors: S. ROJAS-CARO, I. BARIC, C. CAMARENA GRANDE, Mahmut ÇOKER, P. Deegan, M. DIROCCO, F. S. Ezgu, F. FEILLET, V. MALINOVA, E. MENGEL, E. Murphy, J. PASTOR ROSADO, Y. RAHMAN, M. SCARPA, K. O. SCHWAB, V. SMOLKA, J. TAYBERT, V. VALAYANNOPOULOS, Y. YANG, A. QUINN

50th International Liver Congress of the European-Association-for-the-Study-of-the-Liver, Austria, International, Verbal, Summary Text, 2015-2015, WoS, vol 62, pp S811-S811

DOI: 10.1016/s0168-8278(15)31407-0

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