EFFICACY AND SAFETY OF SEBELIPASE ALFA IN CHILDREN AND ADULTS WITH LYSOSOMAL ACID LIPASE DEFICIENCY: RESULTS OF A PHASE 3 TRIAL
Bildiriler > Özet Bildiri · 2015
Yazarlar: S. ROJAS-CARO, I. BARIC, C. CAMARENA GRANDE, Mahmut ÇOKER, P. Deegan, M. DIROCCO, F. S. Ezgu, F. FEILLET, V. MALINOVA, E. MENGEL, E. Murphy, J. PASTOR ROSADO, Y. RAHMAN, M. SCARPA, K. O. SCHWAB, V. SMOLKA, J. TAYBERT, V. VALAYANNOPOULOS, Y. YANG, A. QUINN
50th International Liver Congress of the European-Association-for-the-Study-of-the-Liver, Avusturya, Uluslararası, Sözlü Sunum, Özet Bildiri, 2015-2015, Wos, cilt 62, ss S811-S811