EFFICACY AND SAFETY OF SEBELIPASE ALFA IN CHILDREN AND ADULTS WITH LYSOSOMAL ACID LIPASE DEFICIENCY: RESULTS OF A PHASE 3 TRIAL

Bildiriler > Özet Bildiri · 2015

Yazarlar: S. ROJAS-CARO, I. BARIC, C. CAMARENA GRANDE, Mahmut ÇOKER, P. Deegan, M. DIROCCO, F. S. Ezgu, F. FEILLET, V. MALINOVA, E. MENGEL, E. Murphy, J. PASTOR ROSADO, Y. RAHMAN, M. SCARPA, K. O. SCHWAB, V. SMOLKA, J. TAYBERT, V. VALAYANNOPOULOS, Y. YANG, A. QUINN

50th International Liver Congress of the European-Association-for-the-Study-of-the-Liver, Avusturya, Uluslararası, Sözlü Sunum, Özet Bildiri, 2015-2015, Wos, cilt 62, ss S811-S811

DOI: 10.1016/s0168-8278(15)31407-0

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