P1211 : Efficacy and safety of sebelipase alfa in children and adults with lysosomal acid lipase deficiency: Results of a phase 3 trial
Conference paper > Summary Text
Authors: S. Rojas-Caro, I. Baric, C. Camarena Grande, M. Coker, P. Deegan, M. DiRocco, F.S. Ezgu, F. Feillet, V. Malinova, E. Mengel, E. Murphy, J. Pastor Rosado, Y. Rahman, M. Scarpa, K.O. Schwab, V. Smolka, J. Taybert, V. Valayannopoulos, Y. Yang, A. Quinn
Journal of Hepatology, , , International, Summary Text, WoS, vol 62, pp S811-S811